Background: Lenvatinib is the latest addition to the treatment options for radioactive iodine (RAI)-refractory differentiated thyroid carcinoma (DTC). This study assessed the efficacy of lenvatinib in real-world practice and identified prognostic biomarkers for survival outcomes.
Methods: A multicenter cohort study was conducted in 43 patients receiving lenvatinib, as 1st-line or 2nd-line after sorafenib, for RAI-refractory DTC. Progression-free survival (PFS) was evaluated according to various clinical factors including thyroglobulin doubling time (TgDT), tumor volume DT (TVDT), and tumor growth slope (TGS, slope of tumor change rate).
Results: Thirty-two patients were previously treated with sorafenib. Patients were treated with lenvatinib for 14 months (median) and the median starting dose was 20 mg with reduction to a maintenance dose of 10mg during follow-up. The median PFS was 21.8 months and median OS was not reached. Disease control rate was 97.7% with time to the first objective response of 3.8 months. The PFS according to previous sorafenib treatment, metastatic sites, or maintenance dose did not exhibit any difference. However, TGS measured before (TGSpre) and after (TGSpost) the initiation of lenvatinib were associated with PFS (TGSpre p=0.003;TGSpost p=0.036). Other factors associated with PFS were the sum of the largest diameters of target lesions (p=0.043) and TgDT (p=0.024). However, TVDT calculated before (TVDTpre) and after (TVDTpost) lenvatinib treatment did not portend any impact on PFS (p=0.923 and p=0.966, respectively). Withdrawal of lenvatinib occurred in 21 patients with 7 patients due to lenvatinib-induced adverse events (AEs). AEs of any grade were reported in all patients and AEs of grade 3-4 occurred in 13.9%. The most common AE was hypertension.
Conclusions: Our results support the efficacy of lenvatinib for patients with RAI-refractory DTCs. Measuring the TgDT and TGS can assist in predicting the clinical outcomes in these patients. Although AEs occur frequently, most of them were manageable.